FREEDOMS II

Fingolimod

FREEDOMS II independently confirmed the relapse and MRI efficacy of fingolimod 0.5 mg versus placebo.

Phase
Phase III
Population
Relapsing-remitting multiple sclerosis (RRMS)
Controlled period
Jun 2006 — Jun 2011

What was compared

RandomizedDouble-blindPlacebo-controlledMulticenter
Intervention

Fingolimod 0.5 mg

Orally once daily

n=358
Comparator

Placebo

Matching oral capsule once daily

n=355

Additional randomized arm

Fingolimod 1.25 mg

Orally once daily; later switched to 0.5 mg by amendmentn=370
1,083 randomized24 months controlled phase

Primary endpoint

Prespecified outcome

Annualized relapse rate

24 months

Outcome figure

Primary endpoint results

Intervention Comparator or reference

Annualized relapse rate

Relapses per participant-year

24 months
Fingolimod 0.5 mg
0.21
Placebo
0.40

48% lower relapse rate; rate ratio 0.52 (95% CI 0.40–0.66; P<0.0001).

Selected secondary outcomes

Brain volume

Percentage brain-volume loss favored fingolimod.

Disability progression

The confirmatory disability endpoint was not significant.

Study population

Randomized
1,083 randomized
Age
18–55 years eligible
Disability
EDSS 0–5.5
Disease definition
Relapsing-remitting multiple sclerosis

Who entered the trial

Key inclusion criteria

  • Relapsing-remitting multiple sclerosis
  • Baseline EDSS 0–5.5
  • Protocol-defined recent disease activity

Key exclusion criteria

  • Major immune, malignant, pulmonary, or cardiac disease
  • Pregnancy or breastfeeding
  • Other protocol-defined contraindications to S1P-modulator treatment

Safety signal

  • Lymphopenia, liver-enzyme elevation, herpes zoster, hypertension, first-dose bradycardia, and atrioventricular block were more frequent with fingolimod.
  • Serious adverse events occurred in 15% with fingolimod 0.5 mg and 13% with placebo.

Why it mattered

FREEDOMS II confirmed that the relapse effect of fingolimod was reproducible in a separate large pivotal population.

Important limitation

The trial did not reproduce a significant disability-progression benefit, emphasizing that consistent relapse efficacy does not guarantee concordant disability results.

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